GlaxoSmithKline is close to seeking European approval for a gene therapy drug to fight adenosine deaminase severe combined immune deficiency…
Read More
Pennsylvania baby whose disease prompted improved newborn screenings dies
The little Pennsylvania girl who inspired improved newborn screenings for a rare regenerative disorder has passed away, MyFoxPhilly.com reported. Hannah…
Read More
New hope for Duchenne muscular dystrophy drug
Sarepta Therapeutics Inc’s shares soared 64 percent after it said that the U.S. Food and Drug Administration indicated an alternate…
Read More